ClinicalTrials.Veeva

Menu
N

National Neuromuscular Research Institute | Austin, TX

Research site
(Unclaimed)

Site insights

Top conditions

Top treatments

EDG-5506
PTC857
Pridopidine
NMD670
PXT3003

Curious how this site stacks up to its peers?

Data sourced from clinicaltrials.gov

Work at this site?

CTV for research professionals allows users to enhance their site’s profile, add contact information, and more.

Learn more and claim site

Active trials

6 of 8 total trials

A Phase 3 Study to Evaluate the Efficacy and Safety of Efgartigimod IV in Patients with Acetylcholine Receptor Binding Antibody Seronegative Generalized Myasthenia Gravis (ADAPT SERON)

The primary purpose of this study is to measure the efficacy and safety of efgartigimod intravenously (IV) compared to placebo in participants with A...

Enrolling
Generalized Myasthenia Gravis
Other: Placebo IV
Biological: Efgartigimod IV

The purpose of this study is to evaluate the efficacy and safety of efgartigimod PH20 SC given by a pre-filled syringe in adult patients with ocular...

Enrolling
Myasthenia Gravis, Ocular
Combination Product: Efgartigimod PH20 SC
Other: Placebo PH20 SC

This study is researching an experimental combination treatment with pozelimab and cemdisiran, and cemdisiran monotherapy. The study is focused on pa...

Enrolling
Generalized Myasthenia Gravis
Drug: Pozelimab
Drug: Pozelimab + Cemdisiran

A study of sevasemten (EDG-5506) in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON s...

Enrolling
Becker Muscular Dystrophy
Drug: Placebo
Drug: Sevasemten 10 mg

This Phase 2a study aims to evaluate the efficacy, safety and tolerability of NMD670 vs placebo administered twice a day (BID) for 21 days in ambulat...

Enrolling
Charcot-Marie-Tooth Disease
Drug: NMD670
Drug: Placebo

This study will assess the efficacy and safety of PTC857 treatment in participants diagnosed with ALS.

Active, not recruiting
Amyotrophic Lateral Sclerosis
Drug: Placebo
Drug: PTC857

Trial sponsors

argenx logo
Edgewise Therapeutics logo
N
PTC Therapeutics logo
P
Regeneron Pharmaceuticals logo
P

Clinical trials

Find clinical trialsTrials by location
© Copyright 2024 Veeva Systems