O

Ospedale Pediatrico Bambino Gesu | Dipartimento di Oncoematologia e Terapia Cellulare e Genica

Research site

(Unclaimed)

Location

Piazza Sant'Onofrio 4, Rome, Lazio, Italy

Site insights

Top conditions

Top treatments

Ataluren

ELX

Emapalumab

Tezacaftor

Elexacaftor

Ivacaftor

VX-445

Vancomycin

Ceftazidime

Pegcetacoplan

Data sourced from clinicaltrials.gov

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Active trials

5 of 19 total trials

Atrasentan in Patients With Proteinuric Glomerular Diseases (AFFINITY)

The AFFINITY Study is a phase 2, open-label, basket study to evaluate the efficacy and safety of atrasentan in patients with proteinuric glomerular d...

Active, not recruiting

Immunoglobulin A Nephropathy

Alport Syndrome

Drug: Atrasentan

Long-Term Follow-up Protocol for Participants Treated With Gene-Modified T Cells

This is a prospective study for the long-term follow-up (LTFU) of safety and efficacy for all pediatric and adult participants exposed to Gene-modifi...

Enrolling

Neoplasms

Genetic: Gene-modified (GM) T cell therapy

Long-term Safety and Efficacy of Odevixibat in Patients With Alagille Syndrome (ASSERT-EXT)

The purpose of this study is to assess the long-term safety and effectiveness of odevixibat in participants with Alagille syndrome (ALGS).The partici...

Enrolling

Alagille Syndrome

Drug: Odevixibat

Phase III Study Assessing the Efficacy and Safety of Pegcetacoplan in Patients With C3 Glomerulopathy or Immune-Complex Membranoproliferative Glomerulonephritis (VALIANT)

This is a Phase 3 study to assess the efficacy and safety of twice-weekly subcutaneous (SC) doses of pegcetacoplan compared to placebo in patients wi...

Active, not recruiting

Membranoproliferative Glomerulonephritis (MPGN)

Membranoproliferative Glomerulonephritis

Other: Placebo

Drug: Pegcetacoplan

Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508del

This study will evaluate the long-term safety, efficacy and pharmacodynamics of ELX/TEZ/IVA in participants with cystic fibrosis (CF) with at least 1...

Active, not recruiting

Cystic Fibrosis

Drug: ELX/TEZ/IVA

Drug: IVA