Status and phase
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About
The purpose of this study is to evaluate the safety and tolerability of a single intravenous infusion of AB-1003 in adults diagnosed with limb girdle muscular dystrophy type 2I/R9 (LGMD2I/R9). Participants will be treated in sequential, dose-level cohorts. (Part 1)
Enrollment
Sex
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Inclusion criteria
Exclusion criteria
Primary purpose
Allocation
Interventional model
Masking
10 participants in 3 patient groups, including a placebo group
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Central trial contact
myTomorrows (see link below in reference section); Medical Affairs at AskBio
Data sourced from clinicaltrials.gov
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