A Study to Improve the Awareness of Mucopolysaccharidosis Type II in Brazil

Takeda

Status: Completed

Conditions: Mucopolysaccharidosis (MPS)

Treatments: Other: No Intervention

Study type: Observational

Funder types: Industry

Identifiers

NCT05155488

MACS-2021-021601 (Other Identifier)

TAK-765-5001

Details and patient eligibility

About

The main aims of the study are to learn about the percentage of mucopolysaccharidosis type II (MPS II) in adults in Brazil as well as about the diagnosis process. No study medicines will be provided to participants in this study. The data available for participants diagnosed with MPS II in DATASUS (a database of the Informatics Department of Brazilian Health System) will be reviewed. No clinic visits will be required as part of participation in this study.

Enrollment: 250 patients

Sex: All

Volunteers: No Healthy Volunteers

Inclusion criteria

All MPS II cases of (International Classification of Diseases, 10th revision [ICD-10] E76.1) at any age reported in DATASUS from January 1st, 2008 to September 30th, 2020 will be included.

Exclusion criteria

MPS II cases reported outside this period will be excluded.

Trial design

250 participants in 1 patient group

Participants With MPS II

Description:

Retrospective data of participants diagnosed with MPS II will be collected from the database (DATASUS) from January 1st, 2008 to September 30th, 2020 in this observational study.

Treatment:

Other: No Intervention