Correlation Between Functional Capacity and Functional Capability in Duchenne Muscular Dystrophy

Samsung Medical Center

Status: Enrolling

Conditions: Duchenne Muscular Dystrophy

Treatments: Other: no intervention

Study type: Observational

Funder types: Other

Identifiers

NCT05249361

2022-05-136

Details and patient eligibility

About

This study investigates the correlation between assessments measuring functional capacity and functional capability in patients with Duchenne muscular dystrophy.

Full description

This study is a prospective single-arm observational study, with a total of two visits for one year follow-up.

Enrollment: 48 estimated patients

Sex: All

Ages: 5 to 18 years old

Volunteers: No Healthy Volunteers

Inclusion criteria

1. Children aged 5 to 18 years diagnosed with Duchenne muscular dystrophy through genetic testing
2. Children who understand the contents of this research and can properly conduct the research

Exclusion criteria

1. Requiring daytime ventilator assistance or using invasive mechanical ventilation through tracheostomy (Non-invasive mechanical ventilation such as positive pressure ventilation at night is allowed)
2. History of peripheral nerve damage
3. History of major surgery within 12 weeks or if major surgery is expected during the test period
4. History of central nervous system disorders (eg, cerebral infarction, spinal cord injury)
5. Having difficulties in conducting this study due to cognitive decline.

Trial design

48 participants in 1 patient group

Duchenne Muscular Dystrophy

Description:

Children aged 5 to 18 years with Duchenne muscular dystrophy

Treatment:

Other: no intervention