Expanded Access to Mepsevii

Ultragenyx

Status

Conditions: Sly Syndrome; MPS VII; Mucopolysaccharidosis VII

Treatments: Drug: Mepsevii

Study type: Expanded Access

Funder types: Industry

Identifiers

NCT03775174

UX003-EAP

Details and patient eligibility

About

Individual patient expanded access requests may be considered for patients who have no other treatment options

Full description

Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies. For full details, please visit the links provided below.

Sex: All

Volunteers: No Healthy Volunteers

Inclusion criteria

-

Exclusion criteria

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