Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

LogicBio Therapeutics

Status: Active, not recruiting

Conditions: Methylmalonic Acidemia

Treatments: Drug: hLB-001

Study type: Observational

Funder types: Industry

Identifiers

NCT05506254

LB-001LT

Details and patient eligibility

About

This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001

Full description

Patients will be followed for a period of 15 years which includes the duration of time that the patient was in the treatment study.

Enrollment: 4 patients

Sex: All

Volunteers: No Healthy Volunteers

Inclusion criteria

• Participant has previously participated in a LogicBio clinical trial and received hLB-001.

Exclusion criteria

• None

Trial design

4 participants in 1 patient group

Patients who have previously received hLB-001

Treatment:

Drug: hLB-001