Natural History Study of MNGIE

Entrada Therapeutics

Status: Suspended

Conditions: Mitochondrial Neurogastrointestinal Encephalomyopathy

Treatments: Other: Non-interventional

Study type: Observational

Funder types: Industry

Identifiers

NCT04245917

ET-NHS-901

Details and patient eligibility

About

Non-interventional, prospective, multicenter, natural history study of patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)

Enrollment: 60 estimated patients

Sex: All

Ages: 5+ years old

Volunteers: No Healthy Volunteers

Inclusion criteria

• Has MNGIE

Exclusion criteria

• Substance abuser

Trial design

60 participants in 1 patient group

MNGIE Patients

Description:

Patients with mitochondrial neurogastrointestinal encephalomyopathy

Treatment:

Other: Non-interventional