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Otoferlin Gene-mediated Hearing Loss Natural History Study

A

Akouos

Status

Enrolling

Conditions

Sensorineural Hearing Loss, Bilateral

Treatments

Other: Natural History Study

Study type

Observational

Funder types

Industry

Identifiers

NCT05572073
AK-OTOF-NHS-002

Details and patient eligibility

About

This is a retrospective and prospective longitudinal study in participants with Otoferlin Gene-Mediated Hearing Loss.

Enrollment

150 estimated patients

Sex

All

Ages

Under 44 years old

Volunteers

No Healthy Volunteers

Inclusion criteria

  1. Clinical presentation of bilateral sensorineural hearing loss (SNHL), including auditory neuropathy (AN) / auditory neuropathy spectrum disorder (ANSD) phenotype or medical history of AN / ANSD phenotype earlier in life

  2. Mutation(s) in the otoferlin gene

  3. Able and willing to comply with all study requirements, as evidenced by successful completion of the informed consent (and assent, if applicable) process

    Additional Criteria for Inclusion in the Prospective Phase:

  4. Presence of OAE / CM and absent / abnormal ABRs in at least one ear (that does not have a cochlear implant) within 12 months prior to or at the Month 0 visit

Exclusion criteria

  1. Unwillingness or inability of the potential participant and/or legally authorized representative to comply with all protocol requirements

  2. Presence of cochlear nerve deficiency and/or cochlear nerve dysplasia

    Additional Criteria for Exclusion from the Prospective Phase:

  3. Presence of bilateral cochlear implants at the time of record review or planned within the next 6 months

  4. Presence of middle ear or auditory brainstem implant(s) at the time of record review or planned within the next 6 months

  5. Any condition that would not allow the potential participant to complete follow-up assessments during the course of the study and/or, in the opinion of the Investigator, makes the potential participant unsuitable for the study

Note: Potential participants will not be excluded based on their sex, gender, race, or ethnicity

Trial design

150 participants in 2 patient groups

Retrospective
Treatment:
Other: Natural History Study
Prospective
Treatment:
Other: Natural History Study

Trial contacts and locations

10

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Central trial contact

Akouos Clinical Trials

Data sourced from clinicaltrials.gov

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