Status and phase
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About
The purpose of this study is to provide information regarding the long-term safety and pharmacodynamics of ivacaftor treatment in the pediatric population younger than 6 years of age with Cystic Fibrosis (CF) who have a CFTR gating mutation in at least 1 allele and will further explore the efficacy of long-term ivacaftor treatment in this population of patients with CF.
Enrollment
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Inclusion and exclusion criteria
Inclusion Criteria (Ivacaftor Arm):
Inclusion Criteria (Observational Arm):
Exclusion Criteria (Ivacaftor Arm):
Exclusion Criteria: (Observational Arm)
Primary purpose
Allocation
Interventional model
Masking
33 participants in 2 patient groups
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Data sourced from clinicaltrials.gov
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