Study of ORL-1F (L-fucose) in Patients With Leukocyte Adhesion Deficiency Type II

Orpha Labs

Status and phase: Completed; Phase 2; Phase 1

Conditions: Leukocyte Adhesion Deficiency, Type II

Treatments: Drug: L-fucose

Study type: Interventional

Funder types: Industry

Identifiers

NCT03354533

Ladtwo-1

Details and patient eligibility

About

Study of ORL-1F in Patients With Leukocyte Adhesion Deficiency Type II

Enrollment: 4 patients

Sex: All

Ages: Under 18 years old

Volunteers: No Healthy Volunteers

Inclusion criteria

• Diagnosis of Leukocyte Adhesion Deficiency Type II.
• Less than 18 years old.

Exclusion criteria

• Diagnosis of any other disease that is not a manifestation of Leukocyte Adhesion Deficiency Type II.

Trial design

Primary purpose: Treatment

Allocation: N/A

Interventional model: Single Group Assignment

Masking: None (Open label)

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4 participants in 1 patient group

Treatment with ORL-1F - L-fucose

Other group

Treatment:

Drug: L-fucose