Study of ORL-1M (D-mannose) in Patients With CDG-Ib

Orpha Labs

Status and phase: Unknown; Phase 2; Phase 1

Conditions: CDG Ib

Treatments: Drug: ORL-1M - D-mannose

Study type: Interventional

Funder types: Industry

Identifiers

NCT03404869

PMID-1

Details and patient eligibility

About

Study of ORL-1M in Patients With CDG-Ib

Enrollment: 5 estimated patients

Sex: All

Ages: Under 18 years old

Volunteers: No Healthy Volunteers

Inclusion criteria

• Diagnosis of CGD-1b.
• Less than 18 years old.

Exclusion criteria

• Diagnosis of any other disease that is not a manifestation of CGD-1b.

Trial design

Primary purpose: Treatment

Allocation: N/A

Interventional model: Single Group Assignment

Masking: None (Open label)

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5 participants in 1 patient group

Treatment with ORL-1M - D-mannose

Other group

Treatment:

Drug: ORL-1M - D-mannose